实现合乎道德的药物定价:欧洲孤儿基因组疗法基金。

IF 4.6 3区 医学 Q1 BIOCHEMISTRY & MOLECULAR BIOLOGY
Johanna Risse, Merlin Krzemien, Jan Schnalke, Thomas Heinemann
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引用次数: 0

摘要

预计将有越来越多的新型基因组疗法可供罕见或超罕见疾病患者使用。然而,在医疗预算有限的情况下,目前患者平等获得这些孤儿基因组疗法的主要障碍是制造商收取的高昂价格。考虑到伦理定价理论,本文建议实施一种覆盖所有欧洲成员国的定价基础设施,它有可能促进分配公正,同时保持基因组疗法开发的吸引力。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Towards ethical drug pricing: the European Orphan Genomic Therapies Fund
An increasing number of novel genomic therapies are expected to become available for patients with rare or ultra-rare diseases. However, the primary obstacle to equal patient access to these orphan genomic therapies are currently very high prices charged by manufacturers in the context of limited healthcare budgets. Taking into account ethical pricing theories, the paper proposes the implementation of a pricing infrastructure covering all European member states, which has the potential to promote distributive justice while maintaining the attractiveness of genomic therapy development.
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来源期刊
Gene Therapy
Gene Therapy 医学-生化与分子生物学
CiteScore
9.70
自引率
2.00%
发文量
67
审稿时长
4-8 weeks
期刊介绍: Gene Therapy covers both the research and clinical applications of novel therapeutic techniques based on a genetic component. Over the last few decades, significant advances in technologies ranging from identifying novel genetic targets that cause disease through to clinical studies, which show therapeutic benefit, have elevated this multidisciplinary field to the forefront of modern medicine.
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