亨廷顿舞蹈症临床试验最新进展：2024年2月

IF 2.1 Q3 NEUROSCIENCES

Journal of Huntington's disease Pub Date : 2024-01-01 DOI:10.3233/JHD-240017

Carlos Estevez-Fraga, Sarah J Tabrizi, Edward J Wild

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引用次数: 0

摘要

在本期《亨廷顿氏病临床试验最新进展》中，我们将介绍VICO Therapeutics公司正在进行的项目以及最近终止的VIBRANT-HD临床试验。我们还讨论了 uniQure 的 AMT-130 项目和 PTC therapeutics 的 PTC518 试验的最新进展，并列出了目前所有已注册和正在进行的亨廷顿病临床试验。

本文章由计算机程序翻译，如有差异，请以英文原文为准。

查看原文本刊更多论文

Huntington's Disease Clinical Trials Corner: March 2024.

In this edition of the Huntington's Disease Clinical Trials Update, we expand on the ongoing program from VICO Therapeutics and on the recently terminated VIBRANT-HD clinical trials. We also discuss updates from uniQure's AMT-130 program and PTC therapeutics' trial of PTC518 and list all currently registered and ongoing clinical trials in Huntington's disease.

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来源期刊

Journal of Huntington's disease NEUROSCIENCES-

CiteScore

4.80

自引率

9.70%

发文量