P037:多中心随机三期临床试验(HURCULES)的设计,评估 OTL-203 在 MPS-IH 与异体造血干细胞移植中的应用

Paul Harmatz , Robert Wynn , Ashish Gupta , Sandhya Kharbanda , Caroline Lindemans , Rebecca Ahrens-Nicklas , Peter van Hasselt , Troy Lund , Timothy Olson , Francesca Tucci , Leonie Martin , Nathalie Boeglin , Jean Brooks , Su Syonmez , Laura Campbell , Simon Jones , Paul Orchard , Maria Ester Bernardo
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P037: Design of a multi-center randomized phase 3 clinical trial (HURCULES) evaluating OTL-203 in MPS-IH vs allogeneic hematopoietic stem cell transplantation
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