Jason H Williams, Kai H Liao, Donghua Yin, Xu Meng
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引用次数: 0
摘要
尽管在方法学方面取得了巨大进步,并努力实现数据生成和报告的一致性最佳实践,但解释 mAb 产品的免疫原性结果并预测其临床后果仍然困难重重。为此,临床药理学科的贡献在很大程度上仅限于根据抗药抗体(ADA)状态对药代动力学(PK)概况进行描述性比较,或在群体 PK 设置中测试作为协变量的 ADA 的重要性,这与小分子药物研究内在/外在因素对药物处置影响的做法类似。我们需要一个 mAb 药物处置框架来捕捉 ADA 的形成动态以及药物与 ADA 和靶点的相互作用,将其作为药物分布和消除的一部分。在这里,我们描述了这样一个框架,并根据阿达木单抗治疗患者的 3 期试验中的 PK、ADA 和临床反应数据对其进行了检验。所提出的框架提供了对剂量、靶点亲和力和药物/ADA分析物形式如何影响ADA反应表现的一般理解,包括其检测和药物处置及有效性的改变。此外,举例来说,通过预测一种 PCSK9 抑制剂后期试验中 ADA 发生率和滴度的发展、对药物处置的影响、与靶点的相互作用以及对低密度脂蛋白胆固醇的下游降低作用,证明了该框架在剂量考虑方面的实用性。
Implications of Immunogenicity Testing for Therapeutic Monoclonal Antibodies: A Quantitative Pharmacology Framework.
The interpretation of immunogenicity results for a mAb product and prediction of its clinical consequences remain difficult, despite enormous advances in methodologies and efforts toward the best practice for consistent data generation and reporting. To this end, the contribution from the clinical pharmacology discipline has been largely limited to comparing descriptively the pharmacokinetic (PK) profiles by antidrug antibodies (ADA) status or testing the significance of ADA as a covariate in a population PK setting, similar to the practice for small-molecule drugs in investigating the effect of an intrinsic/extrinsic factor on the drug disposition. There is a need for a mAb disposition framework that captures the dynamics of ADA formation and drug's interactions with the ADA and target as parts of the drug distribution and elimination. Here we describe such a framework and examine it against the PK, ADA, and clinical response data from a phase 3 trial in patients treated with adalimumab. The proposed framework offered a generalized understanding of how the dose, target affinity, and drug/ADA analyte forms affects the manifestation of ADA response with regard to its detections and alterations of drug disposition and effectiveness. Furthermore, as an example, its utility for dose considerations was demonstrated through predicting for late-stage trials of a PCSK9 inhibitor in terms of development in ADA incidence and titers, and consequences on the drug disposition, interaction with target, and downstream lowering effect on LDL-C.
期刊介绍:
The AAPS Journal, an official journal of the American Association of Pharmaceutical Scientists (AAPS), publishes novel and significant findings in the various areas of pharmaceutical sciences impacting human and veterinary therapeutics, including:
· Drug Design and Discovery
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