Lanyan Fang, Yuqing Gong, Andrew C Hooker, Viera Lukacova, Amin Rostami-Hodjegan, Mark Sale, Stella Grosser, Rebeka Jereb, Rada Savic, Carl Peck, Liang Zhao
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引用次数: 0
摘要
随着模型综合证据(MIE)在仿制药开发和监管应用中的作用不断发展,有必要改进模型共享、接受以及与 FDA 的沟通。模型主文件(MMF)是指一个定量模型或建模平台,经过充分的模型验证和确认,被认定为可共享的知识产权,可用于监管目的。MMF 为监管机构可接受的建模实践提供了一个框架,业界和美国食品药品管理局 (FDA) 可以放心地使用该框架来支持 MIE。2022 年,FDA 和复杂仿制药研究中心 (CRCG) 举办了一次虚拟公开研讨会,讨论利用建模方法支持仿制药产品开发的最佳实践。本报告总结了题为 "模型共享、接受以及与 FDA 的沟通 "的研讨会的发言和小组讨论。研讨会和本报告将作为启动讨论的开端,以进一步探讨多用途集成框架的实用性,以及在药物开发和监管申报中利用多用途集成框架的最佳实践。在整个研讨会期间,MMF 的潜在优势得到了模型开发者、行业和 FDA 的认可。为了促进对 MMF 的统一理解,并建立应用 MMF 的最佳实践,利益相关者之间的进一步对话与合作势在必行。为此,后续研讨会将于 2024 年 5 月 2-3 日在马里兰州罗克维尔举行,旨在深入探讨 MMF 在涉及建模和模拟方法的监管申请中的实际应用和最佳实践。
The Role of Model Master Files for Sharing, Acceptance, and Communication with FDA.
With the evolving role of Model Integrated Evidence (MIE) in generic drug development and regulatory applications, the need for improving Model Sharing, Acceptance, and Communication with the FDA is warranted. Model Master File (MMF) refers to a quantitative model or a modeling platform that has undergone sufficient model Verification & Validation to be recognized as sharable intellectual property that is acceptable for regulatory purposes. MMF provides a framework for regulatorily acceptable modeling practice, which can be used with confidence to support MIE by both the industry and the U.S. Food and Drug Administration (FDA). In 2022, the FDA and the Center for Research on Complex Generics (CRCG) hosted a virtual public workshop to discuss the best practices for utilizing modeling approaches to support generic product development. This report summarizes the presentations and panel discussions of the workshop symposium entitled "Model Sharing, Acceptance, and Communication with the FDA". The symposium and this report serve as a kick-off discussion for further utilities of MMF and best practices of utilizing MMF in drug development and regulatory submissions. The potential advantages of MMFs have garnered acknowledgment from model developers, industries, and the FDA throughout the workshop. To foster a unified comprehension of MMFs and establish best practices for their application, further dialogue and cooperation among stakeholders are imperative. To this end, a subsequent workshop is scheduled for May 2-3, 2024, in Rockville, Maryland, aiming to delve into the practical facets and best practices of MMFs pertinent to regulatory submissions involving modeling and simulation methodologies.
期刊介绍:
The AAPS Journal, an official journal of the American Association of Pharmaceutical Scientists (AAPS), publishes novel and significant findings in the various areas of pharmaceutical sciences impacting human and veterinary therapeutics, including:
· Drug Design and Discovery
· Pharmaceutical Biotechnology
· Biopharmaceutics, Formulation, and Drug Delivery
· Metabolism and Transport
· Pharmacokinetics, Pharmacodynamics, and Pharmacometrics
· Translational Research
· Clinical Evaluations and Therapeutic Outcomes
· Regulatory Science
We invite submissions under the following article types:
· Original Research Articles
· Reviews and Mini-reviews
· White Papers, Commentaries, and Editorials
· Meeting Reports
· Brief/Technical Reports and Rapid Communications
· Regulatory Notes
· Tutorials
· Protocols in the Pharmaceutical Sciences
In addition, The AAPS Journal publishes themes, organized by guest editors, which are focused on particular areas of current interest to our field.