Shababa T. Masoud, Hoang Nguyen, Claire Discenza, David Joy, Jeffrey Simms, Iris Lo, You Young Chun, Julia Holtzman, Khishigjaw Tsogtbaatar, Amy Wing-Sze Leung, Isabel Becerra, Elliot Thomsen, Audrey Gill, Yashas Rajendra, Alexander Seay, Mohammad Jafarnejad, Anna I. Bakardjiev, M. E. Calvert, Cathal S. Mahon, Robert Thorne, Steven Chessler, Kirk Henne, Pascal Sanchez, A. Arguello
{"title":"ETV:SGSH 是 SGSH 的脑酶运输载体,可改善 MPS IIIA 小鼠的溶酶体和小胶质细胞形态、退化和认知行为","authors":"Shababa T. Masoud, Hoang Nguyen, Claire Discenza, David Joy, Jeffrey Simms, Iris Lo, You Young Chun, Julia Holtzman, Khishigjaw Tsogtbaatar, Amy Wing-Sze Leung, Isabel Becerra, Elliot Thomsen, Audrey Gill, Yashas Rajendra, Alexander Seay, Mohammad Jafarnejad, Anna I. Bakardjiev, M. E. Calvert, Cathal S. Mahon, Robert Thorne, Steven Chessler, Kirk Henne, Pascal Sanchez, A. Arguello","doi":"10.1016/j.ymgme.2023.107954","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"25 11","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"ETV:SGSH, a brain-penetrant enzyme transport vehicle for SGSH, improves lysosomal and microglial morphology, degeneration and cognitive behavior in MPS IIIA mice\",\"authors\":\"Shababa T. Masoud, Hoang Nguyen, Claire Discenza, David Joy, Jeffrey Simms, Iris Lo, You Young Chun, Julia Holtzman, Khishigjaw Tsogtbaatar, Amy Wing-Sze Leung, Isabel Becerra, Elliot Thomsen, Audrey Gill, Yashas Rajendra, Alexander Seay, Mohammad Jafarnejad, Anna I. Bakardjiev, M. E. Calvert, Cathal S. Mahon, Robert Thorne, Steven Chessler, Kirk Henne, Pascal Sanchez, A. Arguello\",\"doi\":\"10.1016/j.ymgme.2023.107954\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":504050,\"journal\":{\"name\":\"Molecular Genetics and Metabolism\",\"volume\":\"25 11\",\"pages\":\"\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2024-02-01\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"Molecular Genetics and Metabolism\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://doi.org/10.1016/j.ymgme.2023.107954\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2023.107954","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}
ETV:SGSH, a brain-penetrant enzyme transport vehicle for SGSH, improves lysosomal and microglial morphology, degeneration and cognitive behavior in MPS IIIA mice