{"title":"C07利用CRISPRI平台评估HD风险修饰因子在诱导多能干细胞衍生纹状体神经元CAG重复扩增中的作用","authors":"Ross Ferguson, M. Flower, S. Tabrizi","doi":"10.1136/jnnp-2022-ehdn.51","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":447196,"journal":{"name":"C: Genetic modifiers","volume":"40 1","pages":"0"},"PeriodicalIF":0.0000,"publicationDate":"2022-09-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"C07 A CRISPRI platform to assess the role of HD risk modifiers in CAG repeat expansion in iPSC derived striatal neurons\",\"authors\":\"Ross Ferguson, M. Flower, S. Tabrizi\",\"doi\":\"10.1136/jnnp-2022-ehdn.51\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":447196,\"journal\":{\"name\":\"C: Genetic modifiers\",\"volume\":\"40 1\",\"pages\":\"0\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2022-09-01\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"C: Genetic modifiers\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://doi.org/10.1136/jnnp-2022-ehdn.51\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"\",\"JCRName\":\"\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"C: Genetic modifiers","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1136/jnnp-2022-ehdn.51","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}