基于信使RNA (mRNA)的治疗设计用于治疗原发性纤毛运动障碍

C. Woo, N. Clark, A. Sarode, N. Kaushal, K. Tran, T. Efthymiou, J. Abysalh, A. Allawzi, S. Atarod, K. Khoo, E. Meltzer, A. Barbier, R. Wooster
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A Messenger RNA (mRNA)-Based Therapeutic Designed to Treat Primary Ciliary Dyskinesia
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