直到我儿子叫我爸爸:寻找一种治疗超罕见疾病的方法。

IF 4.6 Q2 MATERIALS SCIENCE, BIOMATERIALS

ACS Applied Bio Materials Pub Date : 2022-12-01 DOI:10.1002/jcph.2154

Sanath Kumar Ramesh

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引用次数: 1

摘要

全世界有4亿患者患有罕见病，其中95%的患者得不到治疗。在这篇文章中，作为一个患有罕见疾病的孩子的父母，作为一个药物开发者，我恳请药理学家把注意力转向这种罕见的、毁灭性的疾病。

本文章由计算机程序翻译，如有差异，请以英文原文为准。

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Until My Son Calls Me Dad: Quest to Find a Treatment for Ultra-Rare Disease.

Rare diseases are affecting 400 million patients worldwide, with 95% of them suffering without treatments. In this article, I make a plea, as a parent of a rare disease kid, and as a drug developer, to turn the attention of pharmacologists to such rare and devastating diseases.

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来源期刊

ACS Applied Bio Materials Chemistry-Chemistry (all)

CiteScore

9.40

自引率

2.10%

发文量

464