Melissa Lah , Nicola Longo , Maria Giżewska , Janet Thomas , Amaya Bélanger-Quintana , Ida Vanessa Schwartz , Heidi Peters , Kimberly Ingalls , Zhenming Zhao , Neil Smith , Ania Muntau
{"title":"O09: Sepiapterin responsiveness over 14 days in children and adults with phenylketonuria: Pooled results from three phase 3 clinical trials","authors":"Melissa Lah , Nicola Longo , Maria Giżewska , Janet Thomas , Amaya Bélanger-Quintana , Ida Vanessa Schwartz , Heidi Peters , Kimberly Ingalls , Zhenming Zhao , Neil Smith , Ania Muntau","doi":"10.1016/j.gimo.2026.104294","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":100576,"journal":{"name":"Genetics in Medicine Open","volume":"4 ","pages":"Article 104294"},"PeriodicalIF":0.0000,"publicationDate":"2026-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Genetics in Medicine Open","FirstCategoryId":"1085","ListUrlMain":"https://www.sciencedirect.com/science/article/pii/S2949774426008046","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"2026/3/5 0:00:00","PubModel":"Epub","JCR":"","JCRName":"","Score":null,"Total":0}