Galliano Zanello, Violeta Stoyanova-Beninska, Oxana Iliach, Daniel Scherman, Samantha Parker, David A. Pearce
{"title":"Regulatory sandboxes: A new frontier for rare disease therapies","authors":"Galliano Zanello, Violeta Stoyanova-Beninska, Oxana Iliach, Daniel Scherman, Samantha Parker, David A. Pearce","doi":"10.1016/j.rare.2025.100110","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":101058,"journal":{"name":"Rare","volume":"3 ","pages":"Article 100110"},"PeriodicalIF":0.0000,"publicationDate":"2025-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Rare","FirstCategoryId":"1085","ListUrlMain":"https://www.sciencedirect.com/science/article/pii/S2950008725000547","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}