Correction to “Clinical Outcomes in Patients Switching From Agalsidase Beta to Migalastat: A Fabry Registry Analysis”

IF 4.2 2区医学 Q1 ENDOCRINOLOGY & METABOLISM

Journal of Inherited Metabolic Disease Pub Date : 2025-03-25 DOI:10.1002/jimd.70023

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引用次数: 0

Abstract

A. Pisani, K. M. Wilson, J. L. Batista, et al., “Clinical Outcomes in Patients Switching from Agalsidase Beta to Migalastat: A Fabry Registry Analysis,” Journal of Inherited Metabolic Disease 47, no. 5 (2024): 1080–1095, https://doi.org/10.1002/jimd.12773.

Note: For each outcome, the model includes patients with at least 1 record in each of the pre- and post-switch periods; sample sizes are the same as those shown for Classic and Late-onset patients in Table 2. Each model includes interaction terms to allow slopes to vary by time period (pre/post switch) and phenotype, is adjusted for age at switch date (continuous) and sex, and includes random intercepts. To visually display estimated trajectories over time for each phenotype, estimated values are shown for a male, aged 50 years at the switch date. The slopes of the lines indicate the estimated annual change in the outcome during each time period. Estimated slopes are the same regardless of sex or age.

We apologize for this error.

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来源期刊

Journal of Inherited Metabolic Disease 医学-内分泌学与代谢

CiteScore

9.50

自引率

7.10%

发文量

117

审稿时长

4-8 weeks

期刊介绍： The Journal of Inherited Metabolic Disease (JIMD) is the official journal of the Society for the Study of Inborn Errors of Metabolism (SSIEM). By enhancing communication between workers in the field throughout the world, the JIMD aims to improve the management and understanding of inherited metabolic disorders. It publishes results of original research and new or important observations pertaining to any aspect of inherited metabolic disease in humans and higher animals. This includes clinical (medical, dental and veterinary), biochemical, genetic (including cytogenetic, molecular and population genetic), experimental (including cell biological), methodological, theoretical, epidemiological, ethical and counselling aspects. The JIMD also reviews important new developments or controversial issues relating to metabolic disorders and publishes reviews and short reports arising from the Society''s annual symposia. A distinction is made between peer-reviewed scientific material that is selected because of its significance for other professionals in the field and non-peer- reviewed material that aims to be important, controversial, interesting or entertaining (“Extras”).