P008: A first in human, single arm, open label phase 1/2 study evaluating ECUR-506 in neonatal OTC Deficiency: Initial Observations

Julien Baruteau , Gabriel Cohn , Anil Dhawan , Anupam Chakrapani , Stephanie Grunewald , Molly Abbott , Helen Ashton , Sophie Foxall , Ai Ling Koh , Christos Lazaridis , Havea Navarro-Kennedy , Hamza Patel , Siyamini Sivananthan , Eleni Tamvaki , Katy Vecchiato , Matthew Hall , Karen Kuhn , Thomas White , Barbara Pinho , George Diaz
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P008:首次在人类,单臂,开放标签1/2期研究评估ECUR-506治疗新生儿OTC缺乏症:初步观察
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