Julien Baruteau , Gabriel Cohn , Anil Dhawan , Anupam Chakrapani , Stephanie Grunewald , Molly Abbott , Helen Ashton , Sophie Foxall , Ai Ling Koh , Christos Lazaridis , Havea Navarro-Kennedy , Hamza Patel , Siyamini Sivananthan , Eleni Tamvaki , Katy Vecchiato , Matthew Hall , Karen Kuhn , Thomas White , Barbara Pinho , George Diaz
{"title":"P008: A first in human, single arm, open label phase 1/2 study evaluating ECUR-506 in neonatal OTC Deficiency: Initial Observations","authors":"Julien Baruteau , Gabriel Cohn , Anil Dhawan , Anupam Chakrapani , Stephanie Grunewald , Molly Abbott , Helen Ashton , Sophie Foxall , Ai Ling Koh , Christos Lazaridis , Havea Navarro-Kennedy , Hamza Patel , Siyamini Sivananthan , Eleni Tamvaki , Katy Vecchiato , Matthew Hall , Karen Kuhn , Thomas White , Barbara Pinho , George Diaz","doi":"10.1016/j.gimo.2025.102852","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":100576,"journal":{"name":"Genetics in Medicine Open","volume":"3 ","pages":"Article 102852"},"PeriodicalIF":0.0000,"publicationDate":"2025-01-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Genetics in Medicine Open","FirstCategoryId":"1085","ListUrlMain":"https://www.sciencedirect.com/science/article/pii/S294977442500891X","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}
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