Chris W. Lee, Hui Peng, Aimee R. Herdt, Elizabeth A. Eckman
{"title":"Brain targeted AAV-GALC gene therapy reduces psychosine and extends lifespan in a mouse model of Krabbe disease","authors":"Chris W. Lee, Hui Peng, Aimee R. Herdt, Elizabeth A. Eckman","doi":"10.1016/j.ymgme.2023.107934","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"37 10","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2023.107934","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}