Measurement of glycosaminoglycans in the amniotic fluid of fetuses with mucopolysaccharidoses treated in a phase I clinical trial by in utero enzyme replacement therapy
Sarah P. Young, B. Lianoglou, Akos Herzeg, Beltran Borges, Pranesh Chakraborty, Deeksha Bali, Juan M. Gonzalez, Emma Canepa, Priya S. Kishnani, Jennifer L. Cohen, P. Harmatz, T. Mackenzie
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