Melissa Pille, John M. Avila, So Hyun Park, Cuong Q. Le, Haipeng Xue, F. Haerynck, Lavanya Saxena, Ciaran M. Lee, E. Shpall, Gang Bao, Bart Vandekerckhove, Brian R. Davis
{"title":"Gene Editing based Targeted Integration for Correction of the Wiskott-Aldrich Syndrome","authors":"Melissa Pille, John M. Avila, So Hyun Park, Cuong Q. Le, Haipeng Xue, F. Haerynck, Lavanya Saxena, Ciaran M. Lee, E. Shpall, Gang Bao, Bart Vandekerckhove, Brian R. Davis","doi":"10.1016/j.omtm.2024.101208","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":507212,"journal":{"name":"Molecular Therapy - Methods & Clinical Development","volume":"228 19","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Therapy - Methods & Clinical Development","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.omtm.2024.101208","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}