Using a novel measuring device to objectively evaluate the clinical benefit on ptosis in infantile-onset Pompe disease (IOPD): Results from 145 weeks' avalglucosidase alfa dosing in Mini-COMET participants previously treated with alglucosidase alfa
Priya S. Kishnani, Marguerite C. Weinert, James Davison, A. Brassier, Alexander Broomfield, Yin-Hsiu Chien, S. Hahn, D. Kronn, Satoko Kumada, François Labarthe, Hirotaka Ohki, K. Haack, O. Huynh-Ba, S. Sparks, S. Tammireddy, Tianyue Zhou, S. Prakalapakorn
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