ETV:SGSH, a brain-penetrant enzyme transport vehicle for SGSH, improves lysosomal and microglial morphology, degeneration and cognitive behavior in MPS IIIA mice
Shababa T. Masoud, Hoang Nguyen, Claire Discenza, David Joy, Jeffrey Simms, Iris Lo, You Young Chun, Julia Holtzman, Khishigjaw Tsogtbaatar, Amy Wing-Sze Leung, Isabel Becerra, Elliot Thomsen, Audrey Gill, Yashas Rajendra, Alexander Seay, Mohammad Jafarnejad, Anna I. Bakardjiev, M. E. Calvert, Cathal S. Mahon, Robert Thorne, Steven Chessler, Kirk Henne, Pascal Sanchez, A. Arguello
{"title":"ETV:SGSH, a brain-penetrant enzyme transport vehicle for SGSH, improves lysosomal and microglial morphology, degeneration and cognitive behavior in MPS IIIA mice","authors":"Shababa T. Masoud, Hoang Nguyen, Claire Discenza, David Joy, Jeffrey Simms, Iris Lo, You Young Chun, Julia Holtzman, Khishigjaw Tsogtbaatar, Amy Wing-Sze Leung, Isabel Becerra, Elliot Thomsen, Audrey Gill, Yashas Rajendra, Alexander Seay, Mohammad Jafarnejad, Anna I. Bakardjiev, M. E. Calvert, Cathal S. Mahon, Robert Thorne, Steven Chessler, Kirk Henne, Pascal Sanchez, A. Arguello","doi":"10.1016/j.ymgme.2023.107954","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"25 11","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2023.107954","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}