Molecular Therapy. Nucleic Acids

Molecular Therapy Nucleic Acids is an international, open-access journal that publishes high-quality research in nucleic-acid-based therapeutics to treat and correct genetic and acquired diseases. It is the official journal of the American Society of Gene & Cell Therapy and is built upon the success of Molecular Therapy. The journal focuses on gene- and oligonucleotide-based therapies and publishes peer-reviewed research, reviews, and commentaries. Its impact factor for 2022 is 8.8. The subject areas covered include the development of therapeutics based on nucleic acids and their derivatives, vector development for RNA-based therapeutics delivery, utilization of gene-modifying agents like Zn finger nucleases and triplex-forming oligonucleotides, pre-clinical target validation, safety and efficacy studies, and clinical trials.

《分子疗法核酸》是一本国际开放获取期刊，致力于发表治疗和纠正遗传性疾病和获得性疾病的高质量基于核酸的疗法研究。作为美国基因与细胞治疗学会的官方期刊，它建立在分子治疗的成功基础之上，专注于基因和寡核苷酸疗法的研究与发表。该杂志发表同行评审的研究、评论和评论，其2022年影响因子高达8.8。涵盖的主题领域包括基于核酸及其衍生物的疗法开发、基于RNA的疗法递送的载体开发、锌指核酸酶和三链体形成寡核苷酸等基因修饰剂的利用、临床前靶标验证、安全性和功效研究以及临床试验。