{"title":"全国腺相关病毒载体基因治疗临床实践综述——脊髓性肌肉萎缩症基因治疗的现状及临床实践障碍","authors":"Masayoshi Nakakuni, M. Onodera","doi":"10.3999/jscpt.53.6_217","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":14602,"journal":{"name":"JAPANESE JOURNAL OF CLINICAL PHARMACOLOGY AND THERAPEUTICS","volume":" ","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2022-11-30","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":"{\"title\":\"National Survey on Clinical Practice of Gene Therapy using Adeno-associated Virus Vector ―The Actual Status and Hurdle on Clinical Practice in Gene Therapy for Spinal Muscular Atrophy―\",\"authors\":\"Masayoshi Nakakuni, M. Onodera\",\"doi\":\"10.3999/jscpt.53.6_217\",\"DOIUrl\":null,\"url\":null,\"abstract\":\"\",\"PeriodicalId\":14602,\"journal\":{\"name\":\"JAPANESE JOURNAL OF CLINICAL PHARMACOLOGY AND THERAPEUTICS\",\"volume\":\" \",\"pages\":\"\"},\"PeriodicalIF\":0.0000,\"publicationDate\":\"2022-11-30\",\"publicationTypes\":\"Journal Article\",\"fieldsOfStudy\":null,\"isOpenAccess\":false,\"openAccessPdf\":\"\",\"citationCount\":\"0\",\"resultStr\":null,\"platform\":\"Semanticscholar\",\"paperid\":null,\"PeriodicalName\":\"JAPANESE JOURNAL OF CLINICAL PHARMACOLOGY AND THERAPEUTICS\",\"FirstCategoryId\":\"1085\",\"ListUrlMain\":\"https://doi.org/10.3999/jscpt.53.6_217\",\"RegionNum\":0,\"RegionCategory\":null,\"ArticlePicture\":[],\"TitleCN\":null,\"AbstractTextCN\":null,\"PMCID\":null,\"EPubDate\":\"\",\"PubModel\":\"\",\"JCR\":\"Q4\",\"JCRName\":\"Medicine\",\"Score\":null,\"Total\":0}","platform":"Semanticscholar","paperid":null,"PeriodicalName":"JAPANESE JOURNAL OF CLINICAL PHARMACOLOGY AND THERAPEUTICS","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.3999/jscpt.53.6_217","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"Q4","JCRName":"Medicine","Score":null,"Total":0}
National Survey on Clinical Practice of Gene Therapy using Adeno-associated Virus Vector ―The Actual Status and Hurdle on Clinical Practice in Gene Therapy for Spinal Muscular Atrophy―