依地苯酮——一种治疗遗传性视神经病变的新药

D. Szumny, K. Czajor, M. Mulak
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引用次数: 0

摘要

利伯氏遗传性视神经病变是一种由线粒体DNA突变引起的罕见疾病。它最常见于年轻男性,可在短时间内导致严重的永久性视力丧失。这种情况没有特殊的治疗方法。依地苯酮是一种用于利伯氏遗传性视神经病变患者的药物,可以改善或阻止视力的恶化。增加接受治疗的人数和治疗的持续时间将使将来能够回答这个问题,即这种药物在更大的患者群体中是否有效和安全。
本文章由计算机程序翻译,如有差异,请以英文原文为准。
Idebenone – a new drug for patients with Leber's hereditary optic neuropathy
Leber's Hereditary Optic Neuropathy is a rare disease caused by a mutation in the mitochondrial DNA. It appears most often in young men, leading to profound, permanent loss of vision in a short time. There is no specific treatment for this condition.Idebenone is a medicine that administered to patients with Leber's hereditary optic neuropathy improves or stops the deterioration of vision. Increasing the number of people during therapy and the duration of treatment will allow in the future to answer the question, whether this drug is effective and safe in a larger group of patients.
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