C. Kim, S. Tian, R. Zahigian, A. Elbert, S. Charman, S. Carr, D. Nazareth
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Real-world effects of lumacaftor/ivacaftor (LUM/IVA) in people with cystic fibrosis (pwCF): final results of a long-term safety study using US CF Foundation Patient Registry and UK CF Patient Registry data