Treatment Outcome of Risdiplam and Onasemnogene Abeparvovec in an Infant With Spinal Muscular Atrophy Dependent on Prolonged Invasive Ventilation.

IF 1.4 4区医学 Q2 PEDIATRICS

Journal of paediatrics and child health Pub Date : 2025-09-18 DOI:10.1111/jpc.70199

Jia Wei Audrey Lee, Huixin Huang, Furene Sijia Wang, Stacey Kiat Hong Tay

引用次数: 0

查看原文本刊更多论文

利斯地普兰与阿巴伐韦联合应用治疗依赖长时间有创通气的脊髓性肌萎缩症婴儿的疗效。

本文章由计算机程序翻译，如有差异，请以英文原文为准。

求助全文

约1分钟内获得全文求助全文

来源期刊

Journal of paediatrics and child health 医学-小儿科

CiteScore

2.90

自引率

5.90%

发文量

487

审稿时长

3-6 weeks

期刊介绍： The Journal of Paediatrics and Child Health publishes original research articles of scientific excellence in paediatrics and child health. Research Articles, Case Reports and Letters to the Editor are published, together with invited Reviews, Annotations, Editorial Comments and manuscripts of educational interest.