Non-clinical evaluation of 4D-310 in combination with rituximab/sirolimus: A translational study to support adoption of a novel prophylactic immunomodulation regimen in clinical trials in adults with Fabry disease
Melissa A. Calton, Joshua Holter, Caralee J. Schaefer, Theodore Sullivan, Samantha Jensen, Ed Kim, An Song
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期刊介绍:
Molecular Genetics and Metabolism contributes to the understanding of the metabolic and molecular basis of disease. This peer reviewed journal publishes articles describing investigations that use the tools of biochemical genetics and molecular genetics for studies of normal and disease states in humans and animal models.