Robin C. Ryther, Christine Palladino, Sanjeev V Kothare
{"title":"Improvement in symptoms of Rett syndrome with trofinetide beyond clinical trial efficacy assessments: case reports","authors":"Robin C. Ryther, Christine Palladino, Sanjeev V Kothare","doi":"10.1080/23995270.2024.2375191","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":502304,"journal":{"name":"Future Rare Diseases","volume":"20 5","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-07-15","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Future Rare Diseases","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1080/23995270.2024.2375191","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}