Economics, externalities and rare disease

Rare Pub Date : 2024-01-01 DOI:10.1016/j.rare.2024.100036
Carlisle Ford Runge , James Campbell , Carlisle P. Runge , Reena V. Kartha
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Abstract

Special combined efforts addressing rare diseases should apply economic principles and methods to maximize returns to research and investment. Four opportunities exist: (1) exploiting treatment spillovers; (2) encouraging institutional networking and knowledge-sharing; (3) recognizing shared molecular and genetic etiologies; (4) organizing resulting clusters and baskets for scaling trials, research, diagnosis and treatment.

经济学、外差因素与罕见病
应对罕见病的特别联合行动应采用经济原则和方法,使研究和投资回报最大化。目前存在四个机会:(1) 利用治疗的溢出效应;(2) 鼓励机构联网和知识共享;(3) 承认共同的分子和遗传病因;(4) 组织由此产生的集群和篮子,以扩大试验、研究、诊断和治疗的规模。
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