P012: Pegtibatinase, an investigational enzyme replacement therapy for the treatment of classical homocystinuria: Latest findings from the COMPOSE phase 1/2 trial
Can Ficicioglu , Jaya Ganesh , Wendy Smith , Melissa Lah , David Kudrow , Jalé Güner , Sharon McDermott , Sagar Vaidya , Liz Wilkening , Janet Thomas , Harvey Levy
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