Melissa P. Wasserstein, F. Bonella, Roberto Giugliani, Robin Lachmann, Imre Noth, Maurizio Scarpa, Wim A. Wuyts, Mario Aguiar, Nicole Armstrong, Monica Kumar, Kenneth I Berger
{"title":"Olipudase alfa enzyme replacement therapy reverses interstitial lung disease in adults with acid sphingomyelinase deficiency: Long-term pulmonary outcomes of the ASCEND trial","authors":"Melissa P. Wasserstein, F. Bonella, Roberto Giugliani, Robin Lachmann, Imre Noth, Maurizio Scarpa, Wim A. Wuyts, Mario Aguiar, Nicole Armstrong, Monica Kumar, Kenneth I Berger","doi":"10.1016/j.ymgme.2023.108075","DOIUrl":null,"url":null,"abstract":"","PeriodicalId":504050,"journal":{"name":"Molecular Genetics and Metabolism","volume":"57 2","pages":""},"PeriodicalIF":0.0000,"publicationDate":"2024-02-01","publicationTypes":"Journal Article","fieldsOfStudy":null,"isOpenAccess":false,"openAccessPdf":"","citationCount":"0","resultStr":null,"platform":"Semanticscholar","paperid":null,"PeriodicalName":"Molecular Genetics and Metabolism","FirstCategoryId":"1085","ListUrlMain":"https://doi.org/10.1016/j.ymgme.2023.108075","RegionNum":0,"RegionCategory":null,"ArticlePicture":[],"TitleCN":null,"AbstractTextCN":null,"PMCID":null,"EPubDate":"","PubModel":"","JCR":"","JCRName":"","Score":null,"Total":0}