C08 Knockout of mismatch repair genes MLH1 and MSH3 ablates expansion of the CAG repeat in a human iPSC model of Huntington’s disease

Joseph Stone, Thomas H. Massey, Nicholas Allen, L. Jones
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在亨廷顿病人类iPSC模型中,敲除错配修复基因MLH1和MSH3可减少CAG重复序列的扩增
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